EP1550463A4
Preparation for facilitating site-specific gene conversion and preparation for gene therapy
8 sheets
Sheet 1 Sheet 2 Sheet 3 Sheet 4 Sheet 5 Sheet 6 Sheet 7 Sheet 8
Every citation, both waysCites: the store holds 2 of 3
| Document | Relation | Office | Category | Cited during | Relevant claims |
|---|---|---|---|---|---|
| WO0197857A1 | Cites | World Intellectual Property Organization (WIPO) | XY | Search report | 15-18 |
| WO0197857A | Cites | World Intellectual Property Organization (WIPO) | – | – | – |
| NAKAMURA, MASAAKI ET AL: "Gene therapy of familiar amyloidotic polyneuropathy (FAP) by RNA/DNA chimera oligonucleotides and single-stranded oligonucleotides", SAGAWA SENTAN KAGAKU GIJUTSU SHINKO ZAIDAN JOSEI KENKYU HOKOKUSHO , VOLUME DATE 2001, 14TH, 29-34 CODEN: SSKHFS; ISSN: 0919-0414, 9 September 2002 (2002-09-09), XP008071036 | Non-patent | – | – | Search report | – |
| WELZ C ET AL: "Nuclear gene targeting using negatively charged liposomes", INTERNATIONAL JOURNAL OF PHARMACEUTICS (KIDLINGTON), vol. 196, no. 2, 10 March 2000 (2000-03-10), pages 251 - 252, XP002407008, ISSN: 0378-5173 | Non-patent | – | – | Search report | – |
| HARTIG R ET AL: "Active nuclear import of single-stranded oligonucleotides and their complexes with non-karyophilic macromolecules.", BIOLOGY OF THE CELL / UNDER THE AUSPICES OF THE EUROPEAN CELL BIOLOGY ORGANIZATION. SEP 1998, vol. 90, no. 5, September 1998 (1998-09-01), pages 407 - 426, XP002407009, ISSN: 0248-4900 | Non-patent | – | – | Search report | – |
| CONNORS L H ET AL: "Tabulation of transthyretin (TTR) variants as of 1/1/2000.", AMYLOID : THE INTERNATIONAL JOURNAL OF EXPERIMENTAL AND CLINICAL INVESTIGATION : THE OFFICIAL JOURNAL OF THE INTERNATIONAL SOCIETY OF AMYLOIDOSIS. MAR 2000, vol. 7, no. 1, March 2000 (2000-03-01), pages 54 - 69, XP008071093, ISSN: 1350-6129 | Non-patent | – | – | Search report | – |
| PALÁCIOS S A ET AL: "Familial amyloidotic polyneuropathy type 1 in Brazil is associated with the transthyretin Val30Met variant.", AMYLOID : THE INTERNATIONAL JOURNAL OF EXPERIMENTAL AND CLINICAL INVESTIGATION : THE OFFICIAL JOURNAL OF THE INTERNATIONAL SOCIETY OF AMYLOIDOSIS. DEC 1999, vol. 6, no. 4, December 1999 (1999-12-01), pages 289 - 291, XP008070909, ISSN: 1350-6129 | Non-patent | – | – | Search report | – |
| BENSON M D: "Familial amyloydotic polyneuropathy", TRENDS IN NEUROSCIENCE, ELSEVIER, AMSTERDAM, NL, vol. 12, 1989, pages 88 - 92, XP002975680, ISSN: 0166-2236 | Non-patent | – | – | Search report | – |
| DATABASE BIOSIS [online] BIOSCIENCES INFORMATION SERVICE, PHILADELPHIA, PA, US; 1990, UENO S ET AL: "A NOVEL VARIANT OF TRANSTHYRETIN TYROSINE-114 TO CYSTEINE DEDUCED FROM THE NUCLEOTIDE SEQUENCES OF GENE FRAGMENTS FROM FAMILIAL AMYLOIDOTIC POLYNEUROPATHY IN JAPANESE SIBLING CASES", XP002407018, Database accession no. PREV199090039554 | Non-patent | – | – | Search report | – |
| DATABASE BIOSIS [online] BIOSCIENCES INFORMATION SERVICE, PHILADELPHIA, PA, US; 1992, UENO SATOSHI ET AL: "Familial amyloid polyneuropathy associated with the transthyretin CYS114 gene in a Japanese kindred", XP002407019, Database accession no. PREV199395041538 | Non-patent | – | – | Search report | – |
| DATABASE BIOSIS [online] BIOSCIENCES INFORMATION SERVICE, PHILADELPHIA, PA, US; April 2000 (2000-04-01), SAKASHITA NAOMI ET AL: "Familial amyloidotic polyneuropathy (ATTR Ser50Ile): The first autopsy case report", XP002407020, Database accession no. PREV200000218987 | Non-patent | – | – | Search report | – |
| GERMAIN D P: "[Fabry disease. Clinical and genetic aspects. Therapeutic perspectives]", LA REVUE DE MÉDECINE INTERNE / FONDÉE ... PAR LA SOCIÉTÉ NATIONALE FRANCAISE DE MÉDECINE INTERNE. DEC 2000, vol. 21, no. 12, December 2000 (2000-12-01), pages 1086 - 1103, XP002407010, ISSN: 0248-8663 | Non-patent | – | – | Search report | – |
| ANDO YUKIO: "ANALYSES OF PATHOGENESIS AND THERAPEUTIC APPROACHES FOR HEREDITARY AMYLOIDOSIS", RINSHO BYORI / JAPANESE JOURNAL OF CLINICAL PATHOLOGY, NIPPON RINSHO BYORI GAKKAI, TOKYO, JP, vol. 51, no. 6, June 2003 (2003-06-01), pages 530 - 535, XP008070908, ISSN: 0047-1860 | Non-patent | – | – | Search report | – |
| ANDO Y: "NEW THERAPEUTIC APPROACHES FOR FAMILIAL AMYLOIDOTIC POLYNEUROPATHY (FAP)", AMYLOID, PARTHENON PUBLISHING GROUP, LANCS, GB, vol. 10, no. SUPPL 1, August 2003 (2003-08-01), pages 55 - 66, XP008059597, ISSN: 1350-6129 | Non-patent | – | – | Search report | – |
| NAKAMURA M ET AL: "Targeted conversion of the transthyretin gene in vitro and in vivo", GENE THERAPY, vol. 11, no. 10, May 2004 (2004-05-01), pages 838 - 846, XP002407011, ISSN: 0969-7128 | Non-patent | – | – | Search report | – |
| DATABASE MEDLINE [online] US NATIONAL LIBRARY OF MEDICINE (NLM), BETHESDA, MD, US; October 2004 (2004-10-01), NAKAMURA MASAAKI ET AL: "[Gene therapy in familial amyloidotic polyneuropathy by single-stranded oligonucleotides (SSOs)]", XP002407021, Database accession no. NLM15624495 | Non-patent | – | – | Search report | – |
| DATABASE EMBASE [online] ELSEVIER SCIENCE PUBLISHERS, AMSTERDAM, NL; 2004, SUHR O B ET AL: "Gene therapy: Lessons learned from liver transplantation for transthyretin-amyloidosis", XP002407022, Database accession no. EMB-2005006687 | Non-patent | – | – | Search report | – |
| DATABASE MEDLINE [online] US NATIONAL LIBRARY OF MEDICINE (NLM), BETHESDA, MD, US; October 2004 (2004-10-01), NAKAMURA MASAAKI ET AL: "Applications of gene therapy for familial amyloidotic polyneuropathy.", XP002407023, Database accession no. NLM15461573 | Non-patent | – | – | Search report | – |
| See also references of WO 2004026343A1 | Non-patent | – | – | Search report | – |
7 members in 5 offices
Priority claims9
| Document | Office | Kind | Date |
|---|---|---|---|
| 2002274926 | Japan | A | |
| 2002274926 | Japan | A | |
| 2002274926 | Japan | – | |
| 0311962 | Japan | W | |
| 0311962 | Japan | W | |
| 2002274926 | – | – | – |
| JP20020274926 | – | – | – |
| JP2003011962 | – | – | – |
| WO2003JP11962 | – | – | – |
Members7
| Document | Office | Kind | |
|---|---|---|---|
| WO2004026343A1 | World Intellectual Property Organization (WIPO) | A1 | |
| AU2003264507A1 | Australia | A1 | |
| AU2003264507A8 | Australia | A8 | |
| EP1550463A1 | European Patent Office (EPO) | A1 | |
| JPWO2004026343A1 | Japan | A1 | |
| US2006258602A1 | United States of America | A1 | |
| EP1550463A4This record | European Patent Office (EPO) | A4 |
11 legal events, as the office reported them to INPADOC
Over the term
Point at a mark for the eventEvents
| Event | Code | |
|---|---|---|
| Application deemed to be withdrawnWithdrawn18D | 18D | |
| Information on the status of an ep patent application or granted ep patentGrantedSTATUS: THE APPLICATION IS DEEMED TO BE WITHDRAWNSTAA | STAA | |
| First examination report despatched17Q | 17Q | |
| Supplementary search report drawn up and despatchedA4 | A4 | |
| Party data changed (applicant data changed or rights of an application transferred)RAP1 | RAP1 | |
| Party data changed (applicant data changed or rights of an application transferred)RAP1 | RAP1 | |
| Request for extension of the european patent (deleted)DAX | DAX | |
| Request for examination filed17P | 17P | |
| Designated contracting statesAK | AK | |
| Request for extension of the european patentAX | AX | |
| Public reference made under article 153(3) epc to a published international application that has entered the european phaseORIGINAL CODE: 0009012PUAI | PUAI |
Numbers
- Publication
- 1550463
- Publication, DOCDB
- 1550463
- Publication, EPODOC
- EP1550463
- Application
- 3797684
- Application, DOCDB
- 03797684
- Application, EPODOC
- EP20030797684
Titles3
- German
- VORBEREITUNGSWEG ZUR ERLEICHTERUNG DER SITUSSPEZIFISCHEN GENUMWANDLUNG UND VORBEREITUNGSWEG FÜR DIE GENTHERAPIE
- English
- PREPARATION FOR FACILITATING SITE-SPECIFIC GENE CONVERSION AND PREPARATION FOR GENE THERAPY
- French
- PREPARATION POUR FACILITER LA CONVERSION GENIQUE SPECIFIQUE DE SITE ET PREPARATION POUR LA THERAPIE GENIQUE
Classification
- CPC, 11
- C12N15/87
- A01K67/0276
- A01K2217/075
- A01K2227/105
- A01K2267/03
- A61K31/7088
- A61K47/42
- A61K48/0041
- A61K48/005
- C12N15/907
- A61P43/00
- IPC, 8
- A61K31 7088
- A61K47 42
- A61K48 00
- A61P43 00
- C12N15 87
- C12N15 90
- A61K9 08
- A61K9 14
Designated states1
- Contracting states, 1
- Türkiye
